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Research & Development

At Orphalan we identify, develop and provide access to innovative treatments for patients with rare diseases.

Developing new treatments and new formulations

Developing a new assay to measure treatment effectiveness

Learn more about the Wilson's Disease Registry

The Wilson's Disease Registry is a secure centralised database which records health data on consenting people with Wilson's Disease (WD) throughout the world.

The collection of accurate de-identified data will be used for patient benefit through a systematic collection of core data outcomes, assessed to be clinically important for physicians and patients by a dedicated scientific advisory board including a patient representative.