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Global reach and expertise in Rare Disease

MA = Marketing Authorisation


Available in 30+ countries


Number of employees


Established dedicated team in 20+ countries including the US and Europe

Over 1000+ patients treated around the world

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Transforming Rare Disease Treatment

We believe patients with a rare disease should have access to innovative treatment that improves their care and positively impacts their lives and those of their loved ones.

Our Work With the Medical Community

Our Research & Development

At Orphalan we strive to develop rare disease treatments to improve patients’ lives.

At Orphalan we identify, develop, and provide access to innovative treatments for patients with rare diseases to make a positive and meaningful difference. We work together by listening to patients and putting them first, which enables us to provide treatments and services that work for them.

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