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We identify, develop and deliver innovative therapies for patients living with rare disease.

At Orphalan we listen to patients and put them at the core of all our work. Our primary focus is on rare, often fatal diseases where current therapeutic options do not exist, are suboptimal, or are associated with severe complications.

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Global reach and expertise in Rare Disease

30

Available in 30+ countries

100

Number of employees

20

Established dedicated team in 20+ countries including the US and Europe
OUR PRODUCT

Over 1000+ patients treated around the world

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OUR MISSION

Transforming Rare Disease Treatment

We believe patients with a rare disease should have access to innovative treatment that improves their care and positively impacts their lives and those of their loved ones.

Our Work With the Medical Community

Our Research & Development

At Orphalan we strive to develop rare disease treatments to improve patients’ lives.

At Orphalan we identify, develop, and provide access to innovative treatments for patients with rare diseases to make a positive and meaningful difference. We work together by listening to patients and putting them first, which enables us to provide treatments and services that work for them.

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COMPANY NEWS

COMPANY NEWS

COMPANY NEWS

COMPANY NEWS